Drug Profile
Research programme: recombinant protein therapeutics - Pharming/Transgenic rabbit models
Alternative Names: Enzyme replacement therapies - Pharming/Transgenic rabbit models; recombinant human-alpha-galactosidase; recombinant human-alpha-glucosidase; rh-alpha-galactosidase; rh-alpha-glucosidaseLatest Information Update: 09 Nov 2015
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At a glance
- Originator Transgenic Rabbit Models
- Developer Pharming Group NV
- Class Alpha-glucosidases; Enzymes; Recombinant proteins
- Mechanism of Action Alpha glucosidase replacements; Alpha-galactosidase replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Research Fabry's disease; Glycogen storage disease type II