Avexitide - Amylyx Pharmaceuticals
Alternative Names: Avexitide acetate; Exendin (9-39)amide; Exendin 9; Exendin 9-39 acetate; Exendin-(9-39); Exendin-9,39Latest Information Update: 12 May 2026
At a glance
- Originator Stanford University
- Developer Cambridge University Hospitals; Eiger BioPharmaceuticals, Inc.; Stanford University
- Class Antihypoglycaemics; Peptide fragments
- Mechanism of Action Glucagon-like peptide-1 receptor antagonists
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Orphan Drug Status
Yes - Hypoglycaemia
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase III Congenital hyperinsulinism; Hypoglycaemia
Most Recent Events
- 05 May 2026 Amylyx Pharmaceuticals initiates an expanded-access programme for Hypoglycaemia in USA
- 11 Mar 2026 Amylyx Pharmaceuticals has patent protection for avexitide
- 08 Aug 2025 Efficacy, adverse event and pharmacodynamic data from a phase II trial in Hypoglycaemia released by Amylyx Pharmaceuticals