Cipaglucosidase alfa - Amicus Therapeutics
Alternative Names: AT B200; cipaglucosidase alfa-atga; Pombiliti; Recombinant-human-acid-alpha-glucosidase-enzyme-Amicus; rhGAA-AmicusLatest Information Update: 02 Jan 2025
At a glance
- Originator Amicus Therapeutics
- Class Alpha-glucosidases; Enzymes
- Mechanism of Action Alpha-glucosidase replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Marketed Glycogen storage disease type II
Most Recent Events
- 02 Jan 2025 Launched for Glycogen storage disease type II (Combination therapy) in Croatia (IV) before January 2025
- 02 Jan 2025 Launched for Glycogen storage disease type II (Combination therapy) in Latvia (IV) before January 2025
- 02 Jan 2025 Launched for Glycogen storage disease type II (Combination therapy) in Switzerland (IV) before January 2024