ATB 200

Drug Profile

ATB 200

Alternative Names: AT GAA; AT-B200/AT2220; ATB 200+chaperone; ATB-200; ATB200/AT2221; rhGAA-Amicus Therapeutics

Latest Information Update: 12 Feb 2018

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At a glance

  • Originator Amicus Therapeutics
  • Class Alpha-glucosidases; Enzymes
  • Mechanism of Action Alpha glucosidase replacements
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Glycogen storage disease type II
  • New Molecular Entity Yes

Highest Development Phases

  • Phase I/II Glycogen storage disease type II

Most Recent Events

  • 07 Aug 2018 Amicus Therapeutics intends to complete a retrospective natural history study in approximately 100 ERT-treated Pompe patients in 2H 2018
  • 26 Jun 2018 Amicus Therapeutics announces intention to conduct meeting with the EMA for the potential regulatory pathway for conditional approval of ATB 200 for Glycogen storage disease type II (Pompe disease) in Europe in 2019
  • 26 Jun 2018 Amicus Therapeutics announces intention to conduct Type-C meeting with the US FDA for Glycogen storage disease type II (Pompe disease) in the third quarter of 2018
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