Fordadistrogene movaparvovec - Pfizer
Alternative Names: BMB-D-001; PF 06939926Latest Information Update: 26 Oct 2025
At a glance
- Originator Bamboo Therapeutics
- Developer Pfizer
- Class Gene therapies
- Mechanism of Action Dystrophin replacements; Gene transference
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Orphan Drug Status
Yes - Duchenne muscular dystrophy
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Discontinued Duchenne muscular dystrophy
Most Recent Events
- 26 Oct 2025 Pfizer terminates a phase Ib trial in Duchenne muscular dystrophy (In children, In adolescents, In adults, In the elderly) in USA (IV) (NCT03362502)
- 21 Oct 2025 Pfizer terminates a phase III trial for Duchenne Muscular Dystrophy (In children, In adolescents, In adults, In the elderly) in USA (NCT05689164)
- 21 Oct 2025 Pfizer terminates phase II trial in Duchenne muscular dystrophy (In children) in the US and Australia (IV) (NCT05429372)