Fordadistrogene movaparvovec - Pfizer
Alternative Names: BMB-D-001; PF 06939926Latest Information Update: 17 Jun 2024
At a glance
- Originator Bamboo Therapeutics
- Developer Pfizer
- Class Gene therapies
- Mechanism of Action Dystrophin replacements; Gene transference
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Discontinued Duchenne muscular dystrophy
Most Recent Events
- 12 Jun 2024 Efficacy and adverse events data from the phase III CIFFREO trial in Duchenne muscular dystrophy released by Pfizer
- 01 May 2024 Discontinued - Phase-III for Duchenne muscular dystrophy (In children) in Russia, Switzerland, Taiwan, USA, South Korea, Japan, France, Canada, Belgium, United Kingdom, Italy, Spain, Australia, Germany, Israel (IV) (Pfizer pipeline July 2024)
- 14 Nov 2023 US FDA granted Rare Pediatric Disease for Duchenne muscular dystrophy, prior to November 2023 (Pfizer website, November 2023)