4D 710
Alternative Names: 4D 710Latest Information Update: 17 Jan 2025
At a glance
- Originator 4D Molecular Therapeutics
- Class Antifibrotics; Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase I/II Cystic fibrosis
Most Recent Events
- 17 Jan 2025 Molecular Therapeutics plans pivotal trial proposal for Cystic fibrosis mid-2025
- 07 Jun 2024 Updated efficacy, adverse event and pharmacodynamic data from a phase I/II AEROW trial in Cystic fibrosis released by 4D Molecular Therapeutics
- 28 Mar 2024 4D 710 receives Orphan Drug status for Cystic fibrosis in USA