Research programme: small molecule therapeutics - Sharp Edge Labs
Alternative Names: chemical chaperone therapeuticsLatest Information Update: 28 Apr 2020
At a glance
- Originator Sharp Edge Labs
- Class Small molecules
- Mechanism of Action Protein folding modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- No development reported Alzheimer's disease; Cystic fibrosis; Dementia; Lysosomal storage diseases; Parkinson's disease
Most Recent Events
- 28 Apr 2020 No recent reports of development identified for research development in Alzheimer's-disease in USA
- 28 Apr 2020 No recent reports of development identified for research development in Cystic-fibrosis in USA
- 28 Apr 2020 No recent reports of development identified for research development in Dementia in USA