Iduronicrin genleukocel-T - Immusoft
Alternative Names: ISP-001; Mucopolysaccharidosis type I therapy - ImmusoftLatest Information Update: 27 Sep 2024
At a glance
- Originator Immusoft Corporation
- Developer Immusoft
- Class Cell therapies; Gene therapies
- Mechanism of Action Cell replacements; Gene transference; Iduronidase replacements
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase I Mucopolysaccharidosis I
Most Recent Events
- 23 Sep 2024 Efficacy, adverse events and pharmacodynamics data from a phase I trial in Mucopolysaccharidosis I released by Immusoft
- 12 Apr 2023 Phase-I clinical trials in Mucopolysaccharidosis I (In adults, In the elderly) in USA (Parenteral) (NCT05682144)
- 02 Sep 2022 US FDA approves IND application for Iduronicrin genleukocel-T (ISP-001) in Mucopolysaccharidosis type I (MPS I)