Either you have JavaScript disabled or your browser does not support Javascript . To work properly, this page requires JavaScript to be enabled.
How to enable JavaScript in your browser?

RGX 501

Next Previous
Drug Profile

RGX 501

Alternative Names: Adeno-Associated Viral Vector Expressing Low-Density Lipoprotein Receptor

Latest Information Update: 07 Sep 2021

Price :
$50 *
Note:
  • Adis is an information provider. We do not sell or distribute actual drugs.
  • Final gross price and currency may vary according to local VAT and billing address.
  • Your purchase entitles you to full access to the information contained in our drug profile at the time of purchase.
  • A link to download a PDF version of the drug profile will be included in your email receipt.

At a glance

  • Originator REGENXBIO
  • Developer REGENXBIO; University of Pennsylvania
  • Class Antihyperlipidaemics; Gene therapies; Proteins
  • Mechanism of Action Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Hyperlipoproteinaemia type IIa
  • New Molecular Entity No
  • Available For Licensing Yes

Highest Development Phases

  • Discontinued Hyperlipoproteinaemia type IIa

Most Recent Events

  • 07 Aug 2020 RGX 501 is available for licensing as of 07 Aug 2020. https://www.regenxbio.com/therapeutic-programs/
  • 07 Aug 2020 Discontinued - Phase-I/II for Hyperlipoproteinaemia type IIa in USA (IV)
  • 09 Jan 2020 Safety data from a phase I/II trial in Hyperlipoproteinaemia-type-IIa released by REGENXBIO

You need to be a logged in or subscribed to view this content

Request demo (opens in a new window)
If your organization or you do not have a subscription, try one of the following: If your organization has a subscription, there are several access options, even while working remotely:
  • Working within your organization’s network
  • with username/password or try to via your institution
  • Persisted access using your organization’s identifier stored in your user browser for 90 days
Back to top