Research programme: CDKL5 program - Amicus Therapeutics/MiaMed
Alternative Names: CDKL5Latest Information Update: 31 Oct 2021
At a glance
- Originator MiaMED
- Developer Amicus Therapeutics
- Class Neuroprotectants
- Mechanism of Action Cyclin-dependent kinase 5 modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- No development reported Neurological disorders