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Mucopolysaccharidosis IIIB therapeutic - Dorphan

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Drug Profile

Mucopolysaccharidosis IIIB therapeutic - Dorphan

Latest Information Update: 06 Sep 2023

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At a glance

  • Originator DORPHAN S.A.
  • Class Imino sugars; Pharmacological chaperones
  • Mechanism of Action Hexosaminidase inhibitors
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • New Molecular Entity Yes
  • Available For Licensing Yes

Highest Development Phases

  • Discontinued Mucopolysaccharidosis III

Most Recent Events

  • 06 Sep 2023 Discontinued - Preclinical for Mucopolysaccharidosis III in Switzerland (unspecified route) (Dorphan website, September 2023)
  • 28 Aug 2020 No recent reports of development identified for preclinical development in Mucopolysaccharidosis-III in Switzerland
  • 15 Jul 2016 Mucopolysaccharidosis IIIB therapeutic - Dorphan is available for licensing as of 15 Jul 2016. http://www.dorphan.com/

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