Mucopolysaccharidosis IVIIB therapeutic - Dorphan
Latest Information Update: 15 Jul 2016
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At a glance
- Originator DORPHAN S.A.
- Class Imino sugars; Pharmacological chaperones
- Mechanism of Action Glycoside hydrolase inhibitors
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
- Available For Licensing Yes
Highest Development Phases
- Preclinical Mucopolysaccharidosis IV
Most Recent Events
- 15 Jul 2016 Mucopolysaccharidosis IVIIB therapeutic - Dorphan is available for licensing as of 15 Jul 2016. http://www.dorphan.com/
- 15 Jul 2016 Preclinical trials in Mucopolysaccharidosis IV in Switzerland (unspecified route)