XN 001
Alternative Names: XN-001Latest Information Update: 12 Sep 2023
At a glance
- Originator XoNovo
- Class Small molecules
- Mechanism of Action Autophagy stimulants
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Discontinued Alzheimer's disease; Muscular dystrophies; Neuronal ceroid lipofuscinosis
Most Recent Events
- 12 Sep 2023 Discontinued - Preclinical for Alzheimer's disease in Israel (unspecified route) (FutuRx pipeline, September 2023)
- 12 Sep 2023 Discontinued - Preclinical for Muscular dystrophies in Israel (unspecified route) (FutuRx pipeline, September 2023)
- 12 Sep 2023 Discontinued - Preclinical for Neuronal ceroid lipofuscinosis in Israel (unspecified route) (FutuRx pipeline, September 2023)