Pegtibatinase - Travere Therapeutics
Alternative Names: htCBS C15S ME-200GS; OT-58; PEG htCBS C15S; PEG modified CBS; TVT-058Latest Information Update: 04 Oct 2024
At a glance
- Originator Orphan Technologies
- Developer Orphan Technologies; Travere Therapeutics
- Class Enzymes
- Mechanism of Action Enzyme replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase III Homocystinuria
Most Recent Events
- 27 Sep 2024 Travere Therapeutics suspends enrollment in the phase III HARMONY trial for Homocystinuria (SC)
- 26 Sep 2024 Travere Therapeutics plans to restart the phase III HARMONY trial for homocystinuria in 2026 (SC)
- 30 Apr 2024 Travere Therapeutics initiates enrolment by invitation in a phase IIIb trial for Homocystinuria (In adolescents, In adults) in USA (SC) (NCT06431893)