Research programme: neurodegenerative amyloid disorder therapeutics - BSIM Therapeutics
Alternative Names: ATTR EYE; ATTR HEART; ATTR PNS/CNSLatest Information Update: 01 Oct 2021
At a glance
- Originator BSIM2
- Developer BSIM Therapeutics; BSIM2
- Class Cardiovascular therapies; Eye disorder therapies; Neuroprotectants; Small molecules
- Mechanism of Action Amyloid inhibitors
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
- Available For Licensing Yes - Amyloid polyneuropathy; Familial amyloidosis
Highest Development Phases
- Research Cardiomyopathies; Cerebrovascular disorders; Eye disorders; Familial amyloid neuropathy
- No development reported Alzheimer's disease
Most Recent Events
- 01 Oct 2021 neurodegenerative amyloid disorder therapeutics is still in early research for familial amyloid neuropathy, familial amyloidotic cardiomyopathy and cerebrovascular and eye disorders associated with transthyretin-related amyloidosis (BSIM Therapeutics pipeline, October 2021)
- 01 Oct 2021 BSIM Therapeutics files for patent protection for AT50, AT40, AT09 and NT60 technologies as of October 2021 (BSIM Therapeutics pipeline; October 2021)
- 01 Oct 2021 Early research in Cerebrovascular disorders in Portugal (unspecified route) as of October 2021 (BSIM Therapeutics pipeline, October 2021)