GB 2064
Alternative Names: GB-2064; PAT 1251Latest Information Update: 10 Oct 2024
At a glance
- Originator PharmAkea Therapeutics
- Developer Galecto Inc
- Class Amines; Antifibrotics; Fluorinated hydrocarbons; Ketones; Phenyl ethers; Pyridines; Pyrrolidines; Small molecules
- Mechanism of Action LOXL2 protein inhibitors
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Discontinued Hepatic fibrosis; Idiopathic pulmonary fibrosis; Myelofibrosis