PF 07055480

Drug Profile

PF 07055480

Alternative Names: AAV cDNA gene therapy - Sangamo Therapeutics; AAV cDNA hF8 gene therapy; AAV cDNA human Factor 8 gene therapy; AAV Factor 8 cDNA gene therapy; AAV Factor 8 cDNA in vivo gene therapy; PF-07055480; Recombinant AAV2/6 Human Factor 8 Gene Therapy - Sangamo Therapeutics; SB-525; SB-525 cDNA gene therapy

Latest Information Update: 08 Mar 2018

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At a glance

  • Originator Sangamo BioSciences
  • Developer Sangamo Therapeutics
  • Class Antihaemorrhagics; Gene therapies
  • Mechanism of Action Factor VIII stimulants; Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Haemophilia A
  • New Molecular Entity No

Highest Development Phases

  • Phase II Haemophilia A

Most Recent Events

  • 08 Mar 2018 Phase-II clinical trials in Haemophilia A in USA (IV) (Pfizer pipeline, March 2018)
  • 07 Jun 2017 PF 07055480 receives Orphan Medicinal Product status for Haemophilia A in European Union
  • 02 Jun 2017 Phase-I/II clinical trials in Haemophilia A in USA (IV) (NCT03061201)
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