Research programme: gene therapies - MeiraGTx
Alternative Names: A-005; AAV2/8-hRKp.RPGRLatest Information Update: 10 Oct 2023
At a glance
- Originator MeiraGTx
- Class Eye disorder therapies; Gene therapies
- Mechanism of Action Gene transference; Platelet-derived growth factor beta receptor antagonists; Vascular endothelial growth factor receptor-2 antagonists
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Amyotrophic lateral sclerosis; Dry age-related macular degeneration; Wet age-related macular degeneration
Most Recent Events
- 01 Oct 2023 Janssen Pharmaceuticals is now called Johnson & Johnson Innovative Medicine (Janssen Pharmaceuticals website, October 2023)
- 28 Jun 2023 No recent reports of development identified for preclinical development in Amyotrophic-lateral-sclerosis in USA (Parenteral)
- 28 Jun 2023 No recent reports of development identified for preclinical development in Dry age-related macular degeneration in USA (Parenteral)