Research programme: RNA based therapeutics - miRecule
Alternative Names: MIR 101; MIR-101 - miRecule; miR-30-5p mimicLatest Information Update: 28 Jun 2025
At a glance
- Originator miRecule
- Class Antineoplastics; Antivirals; MicroRNAs; Oligoribonucleotides; RNA; RNA binding proteins
- Mechanism of Action MicroRNA modulators; RNA interference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- No development reported COVID 2019 infections; Head and neck cancer; HIV infections
Most Recent Events
- 28 Jun 2025 No recent reports of development identified for research development in COVID-2019-infections in USA (Parenteral)
- 28 Jun 2025 No recent reports of development identified for research development in HIV-infections in USA (Parenteral)
- 07 Jun 2021 miRecule has patent protection for RNA chemistry to develop RNA therapeutics before May 2021 (miRecule website, June 2021)