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Research programme: SVP platform-based gene therapeutics - Spark Therapeutics

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Drug Profile

Research programme: SVP platform-based gene therapeutics - Spark Therapeutics

Alternative Names: SVP platform-based factor VIII gene therapy - Spark Therapeutics; SVP platform-based FVIII gene therapy - Spark Therapeutics; SVP-Rapamycin plus FVIII gene therapy - Spark Therapeutics

Latest Information Update: 05 Dec 2023

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At a glance

  • Originator Spark Therapeutics
  • Developer Cartesian Therapeutics; Spark Therapeutics
  • Class Blood coagulation factors; Gene therapies
  • Mechanism of Action Blood coagulation factor replacements; Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • New Molecular Entity No

Highest Development Phases

  • No development reported Haemophilia A

Most Recent Events

  • 18 Jan 2022 Spark Therapeutics terminates its license and option agreement with Cartesian Therapeutics for immune tolerance SVP™ platform technology
  • 28 Jan 2021 No recent reports of development identified for research development in Haemophilia-A in USA (Parenteral)
  • 17 Dec 2019 Spark Therapeutics has been acquired by Roche

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