Drug Profile

Research programme: enzyme replacement therapeutics - SylamoreBio

Latest Information Update: 27 Feb 2026

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At a glance

Originator BioStrategies LC
Developer SylamoreBio
Class Enzymes
Mechanism of Action Enzyme replacements; Heparan sulfate sulfatase replacements; Iduronidase replacements

Orphan Drug Status

Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

No
New Molecular Entity Yes

No development reported Gaucher's disease; Mucopolysaccharidosis I; Mucopolysaccharidosis III

28 Nov 2020 No recent reports of development identified for research development in Gaucher's-disease in USA (IV)
28 Nov 2020 No recent reports of development identified for research development in Gaucher's-disease in USA (Transmucosal)
28 Nov 2020 No recent reports of development identified for research development in Mucopolysaccharidosis-I in USA (IV)

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