Research programme: neurodegenerative gene therapies - MeiraGTx/Weill Cornell Medicine
Latest Information Update: 28 Jan 2021
At a glance
- Originator MeiraGTx; Weill Cornell Medical College
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Neurodegenerative disorders
Most Recent Events
- 28 Jan 2021 No recent reports of development identified for research development in Neurodegenerative-disorders in USA (Parenteral)
- 12 Dec 2016 Early research in Neurodegenerative disorders in USA