Research programme: neurometabolic disease therapeutics - Gain Therapeutics
Latest Information Update: 04 Apr 2023
At a glance
- Originator Gain Therapeutics
- Class Small molecules
- Mechanism of Action Glycoside hydrolase modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Research Gangliosidoses
- No development reported Mucopolysaccharidosis IV
Most Recent Events
- 04 Apr 2023 Early research is ongoing for Gangliosidoses in Spain (Gain Therapeutics pipeline, March 2023)
- 28 Jan 2021 No recent reports of development identified for research development in Gangliosidoses in Spain
- 28 Jan 2021 No recent reports of development identified for research development in Mucopolysaccharidosis-IV in Spain