Drug Profile
Research programme: amino acids therapeutics - Axcella
Alternative Names: DAACS™; Defined Amino Acid CompositionsLatest Information Update: 09 Jan 2017
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At a glance
- Originator Axcella Health
- Class Amino acids peptides and proteins
- Mechanism of Action Amino acid replacements
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical Epilepsy; Muscular atrophy; Myotonic dystrophy; Non-alcoholic fatty liver disease