SB 913
Alternative Names: SB-913Latest Information Update: 30 Mar 2022
Price :
$50 *
At a glance
- Originator Sangamo Therapeutics
- Class Gene therapies; Zinc finger DNA binding proteins
- Mechanism of Action Gene transference; Iduronate sulfatase replacements
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Discontinued Mucopolysaccharidosis II
Most Recent Events
- 22 Feb 2022 Discontinued - Phase-I/II for Mucopolysaccharidosis II in United Kingdom (IV), in January 2021
- 22 Feb 2022 Discontinued - Phase-I/II for Mucopolysaccharidosis II in USA (IV), in January 2021
- 07 May 2021 Sangamo Therapeutics terminated the CHAMPIONS phase I/II trial in Mucopolysaccharidosis II in USA and United Kingdom (IV) (NCT03041324) (EudraCT2018-000192-33)