Research programme: genetic disorder therapeutics - Apollo Therapeutics
Latest Information Update: 28 Mar 2021
At a glance
- Originator Apollo Therapeutics
- Developer Apollo Therapeutics; University of Cambridge
- Class Small molecules
- Mechanism of Action Alpha 1-antitrypsin modulators
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- No development reported Alpha 1-antitrypsin deficiency
Most Recent Events
- 28 Mar 2021 No recent reports of development identified for research development in Alpha-1-antitrypsin-deficiency in United Kingdom
- 22 Feb 2017 Early research in Alpha 1-antitrypsin deficiency in United Kingdom (unspecified route)