Drug Profile

Research programme: antisense therapies - Ionis Pharmaceuticals

Alternative Names: single-stranded RNAi - Ionis; ssRNAi - Ionis

Latest Information Update: 30 May 2024

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At a glance

Originator Ionis Pharmaceuticals
Class Antisense oligonucleotides; Small interfering RNA
Mechanism of Action Protein synthesis inhibitors; RNA inhibitors; RNA interference

Orphan Drug Status

Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

No
New Molecular Entity Yes

31 Dec 2023 Preclinical trials in Metabolic disorders in USA (Parenteral), prior to December 2023
28 May 2023 No recent reports of development identified for research development in Metabolic-disorders in China (Parenteral)
28 May 2023 No recent reports of development identified for research development in Metabolic-disorders in USA (Parenteral)

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