Acoramidis - BridgeBio Pharma
Alternative Names: Acoramidis hydrochloride; AG-10; AG10 hydrochloride; ALXN 2060; Attruby; BBP-265; BEYONTTRA; BeyonttraLatest Information Update: 16 Mar 2026
At a glance
- Originator Stanford University
- Developer Alexion AstraZeneca Rare Disease; Bayer; BridgeBio Pharma; Eidos Therapeutics
- Class Benzoic acids; Ethers; Fluorobenzenes; Pyrazoles; Small molecules
- Mechanism of Action Prealbumin modulators
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Orphan Drug Status
Yes - Amyloidosis
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Marketed Transthyretin-related hereditary amyloidosis
Most Recent Events
- 26 Feb 2026 Launched for Transthyretin-related hereditary amyloidosis in Germany (PO) prior to February 2026
- 21 Jan 2026 Launched for Transthyretin-related hereditary amyloidosis in United Kingdom (PO) prior to January 2026
- 08 Nov 2025 Updated efficacy data from the phase-III ATTRibute-CM trial in Transthyretin-related hereditary amyloidosis released by BridgeBio Pharma