Acoramidis - BridgeBio Pharma
Alternative Names: Acoramidis hydrochloride; AG-10; AG10 hydrochloride; ALXN 2060; Attruby; BBP-265; BEYONTTRA; BeyonttraLatest Information Update: 15 May 2026
At a glance
- Originator Stanford University
- Developer Alexion AstraZeneca Rare Disease; Bayer; BridgeBio Pharma; Eidos Therapeutics
- Class Benzoic acids; Ethers; Fluorobenzenes; Pyrazoles; Small molecules
- Mechanism of Action Prealbumin modulators
-
Orphan Drug Status
Yes - Amyloidosis
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Marketed Transthyretin-related hereditary amyloidosis
Most Recent Events
- 06 May 2026 Registered for Transthyretin-related hereditary amyloidosis in Brazil (PO)
- 06 May 2026 Bayer plans to launch Acoramidis for Transthyretin-related hereditary amyloidosis in Brazil the second half of 2026
- 31 Mar 2026 Efficacy data from a phase III open label extension trial in Transthyretin-related hereditary amyloidosis released by BridgeBio Pharma