Isaralgagene civaparvovec - Sangamo Therapeutics
Alternative Names: ST 920Latest Information Update: 30 Jun 2025
At a glance
- Originator Sangamo Therapeutics
- Class Gene therapies
- Mechanism of Action Alpha-galactosidase replacements; Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
- Available For Licensing Yes
Highest Development Phases
- Phase I/II Fabry's disease
Most Recent Events
- 25 Jun 2025 Efficacy and adverse events data from a phase I/II STAAR trial in Fabry's disease released by Sangamo Therapeutics
- 06 May 2025 Sangamo Therapeutics announces intention to submit BLA to US FDA for Fabry's disease, in the first quarter of 2026
- 06 May 2025 Sangamo Therapeutics anticipates a potential approval and commercial launch as early as the second half of 2026