Research programme: AAV-cDNA gene therapeutics - Sangamo Therapeutics

Drug Profile

Research programme: AAV-cDNA gene therapeutics - Sangamo Therapeutics

Alternative Names: AAV-cDNA gene therapy - Sangamo Therapeutics; ST 920

Latest Information Update: 31 May 2017

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At a glance

  • Originator Sangamo Therapeutics
  • Class Gene therapies
  • Mechanism of Action Alpha-galactosidase stimulants; Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

  • New Molecular Entity No

Highest Development Phases

  • Preclinical Fabry's disease

Most Recent Events

  • 31 May 2018 Sangamo Therapeutics intends to file an IND application with the FDA for Fabry's disease by mid 2018
  • 15 May 2017 Preclinical trials in Fabry's disease in USA (IV,Infusion)
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