Drug Profile
PTI NC 733
Alternative Names: PTI 428/PTI 801/PTI 808; PTI-NC-733Latest Information Update: 29 Feb 2024
Price :
$50
*
At a glance
- Originator Proteostasis Therapeutics
- Developer Kineta
- Class Small molecules
- Mechanism of Action Cystic fibrosis transmembrane conductance regulator modulators
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- No development reported Cystic fibrosis