Drug Profile
GT 0002X
Alternative Names: Aromatic l-amino acid decarboxylase deficiency gene therapy - Gene Therapy Research Institution; GT-0002XLatest Information Update: 28 Sep 2020
Price :
$50
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At a glance
- Originator Gene Therapy Research Institution
- Class Gene therapies
- Mechanism of Action Aromatic-L-amino-acid decarboxylase replacements; Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Aromatic amino acid decarboxylase deficiency
Most Recent Events
- 28 Sep 2020 No recent reports of development identified for clinical-Phase-Unknown development in Aromatic amino acid decarboxylase deficiency in Japan (Parenteral)
- 10 Aug 2017 Clinical trials in Aromatic amino acid decarboxylase deficiency in Japan (Parenteral) (Gene Therapy Research Institution pipeline, August 2017)
- 10 Aug 2017 Gene Therapy Research Institution plans phase I/II trials in 2019 (Gene Therapy Research Institution pipeline, August 2017)