AT 982

Drug Profile

AT 982

Alternative Names: AT-002 - Audentes Therapeutics; AT982

Latest Information Update: 01 Sep 2017

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At a glance

  • Originator Audentes Therapeutics
  • Class Gene therapies
  • Mechanism of Action Alpha glucosidase expression stimulants; Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

  • New Molecular Entity No

Highest Development Phases

  • Phase I/II Glycogen storage disease type II

Most Recent Events

  • 09 May 2018 Audentes Therapeutics plans to file an IND application, for systemic AT 982 for Glycogen storage disease type II, in the fourth quarter of 2018
  • 09 May 2018 Audentes plans a phase I/II proof of concept trial for Glycogen storage disease type II in the first half of 2019
  • 31 Aug 2017 AT 982 is still in preclinical trials for Glycogen storage disease type II in USA (Parenteral/Systemic) (Audentes Therapeutics pipeline, August 2017)
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