Research programme: CNS disorder therapeutics - Amylon Therapeutics
Alternative Names: AT-010 - AmylonLatest Information Update: 26 Jun 2023
At a glance
- Originator ProQR Therapeutics
- Developer Amylon Therapeutics
- Class Antidementias; Neuroprotectants; Oligonucleotides; RNA
- Mechanism of Action Amyloid modulators
-
Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Preclinical App-related cerebroarterial amyloidosis
Most Recent Events
- 26 Jun 2023 CNS disorder therapeutics is still in early research in APP-related cerebroarterial amyloidosis in Netherlands (Amylon Therapeutics pipeline, June 2023)
- 26 Jun 2023 Preclinical trials in App-related cerebroarterial amyloidosis in Netherlands (unspecified route) (Amylon Therapeutics pipeline, June 2023)
- 28 Oct 2021 No recent reports of development identified for research development in App-related-cerebroarterial-amyloidosis in Netherlands