Drug Profile
PRAX 330
Alternative Names: GS967; PRAX-330Latest Information Update: 28 Jan 2018
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At a glance
- Originator Praxis Precision Medicines
- Developer Northwestern University Feinberg School of Medicine; Praxis Precision Medicines
- Class Antiepileptic drugs; Neuroprotectants; Pyridines; Small molecules; Triazoles
- Mechanism of Action Nav1.6 voltage-gated sodium channel inhibitors
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase I Epilepsy
Most Recent Events
- 30 Nov 2017 Phase-I clinical trials in Epilepsy (In volunteers) in Australia (PO)
- 20 Nov 2017 Chemical structure information added
- 03 Nov 2017 Praxis Precision Medicines plans a phase I trial for Epilepsy (In volunteers) in Australia in December 2017 (PO) (ACTRN12617001512314p)