Either you have JavaScript disabled or your browser does not support Javascript . To work properly, this page requires JavaScript to be enabled.
How to enable JavaScript in your browser?

Research programme: ophthalmic gene therapies - Biogen

Next Previous
Search
Drug Profile

Research programme: ophthalmic gene therapies - Biogen

Alternative Names: NSR-ABCA4; NSR-BEST1

Latest Information Update: 28 Apr 2023

Price :
$50 *
Note:
  • Adis is an information provider. We do not sell or distribute actual drugs.
  • Final gross price and currency may vary according to local VAT and billing address.
  • Your purchase entitles you to full access to the information contained in our drug profile at the time of purchase.
  • A link to download a PDF version of the drug profile will be included in your email receipt.

At a glance

  • Originator University of Oxford
  • Developer Biogen; University of Oxford
  • Class Eye disorder therapies; Gene therapies
  • Mechanism of Action Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • New Molecular Entity No

Highest Development Phases

  • No development reported Stargardt disease; Vitelliform macular dystrophy

Most Recent Events

  • 28 Apr 2023 No recent reports of development identified for preclinical development in Vitelliform-macular-dystrophy in United Kingdom (Intraocular)
  • 28 Dec 2021 No recent reports of development identified for preclinical development in Stargardt disease in United Kingdom (Intraocular)
  • 16 Apr 2019 Nightstar Therapeutics plans a phase I/II trial for Vitelliform macular dystrophy in United Kingdom (Intaocular)

You need to be a logged in or subscribed to view this content Request demo

If your organization or you do not have a subscription, try one of the following:
  • Contacting your organization’s admin about adding this content to your AdisInsight subscription
  • Buying a PDF version of any individual profile
  • Request a free trial
If your organization has a subscription, there are several access options, even while working remotely:
  • Working within your organization’s network
  • with username/password or try to via your institution
  • Persisted access using your organization’s identifier stored in your user browser for 90 days
Back to top