Drug Profile
DCR PHXC
Alternative Names: DCR-PHXCLatest Information Update: 11 Dec 2017
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At a glance
- Originator Dicerna Pharmaceuticals
- Class Small interfering RNA
- Mechanism of Action Oxalate modulators; RNA interference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase I Primary hyperoxaluria