Patidistrogene bexoparvovec - Myonexus Therapeutics/Sarepta Therapeutics
Alternative Names: MYO-102; scAAVrh74-tMCK-hSGCA; scAAVrh74.tMCK.hSGCA; SRP-9004Latest Information Update: 28 Jan 2022
At a glance
- Originator Nationwide Children's Hospital
- Developer Myonexus Therapeutics; Nationwide Children's Hospital
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Phase I/II Limb girdle muscular dystrophies
Most Recent Events
- 28 Jan 2022 No recent reports of development identified for phase-I development in Limb-girdle-muscular-dystrophies in USA (IM)
- 09 Jan 2020 MYO 102 is still in clinical trials for Limb girdle muscular dystrophies in USA (Sarepta pipeline, January 2020)
- 02 Jan 2019 MYO 102 receives Orphan Drug status for Sarcoglycanopathies in USA