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Research programme: small molecule therapeutics - Expansion Therapeutics

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Research programme: small molecule therapeutics - Expansion Therapeutics

Latest Information Update: 28 Feb 2025

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At a glance

  • Originator Expansion Therapeutics
  • Class Small molecules
  • Mechanism of Action RNA modulators
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • New Molecular Entity Yes

Highest Development Phases

  • No development reported Myotonic dystrophy

Most Recent Events

  • 28 Feb 2025 No recent reports of development identified for research development in Myotonic dystrophy in USA
  • 03 Feb 2023 Research programme of small molecule therapeutics is still in research development in Myotonic dystrophy in USA (Expansion Therapeutics pipeline, February 2023)
  • 28 Feb 2022 No recent reports of development identified for research development in Myotonic dystrophy in USA

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