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Research programme: gene therapies - Generation Bio

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Drug Profile

Research programme: gene therapies - Generation Bio

Latest Information Update: 28 Nov 2024

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At a glance

  • Originator Generation Bio
  • Class Antihaemorrhagics; Eye disorder therapies; Gene therapies; Hepatoprotectants
  • Mechanism of Action Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • New Molecular Entity No

Highest Development Phases

  • Preclinical Eye disorders
  • No development reported Gaucher's disease; Haemophilia A; Hepatolenticular degeneration; Inborn genetic disorders; Liver disorders; Phenylketonuria; Stargardt disease; Wet age-related macular degeneration

Most Recent Events

  • 28 Nov 2024 No recent reports of development identified for preclinical development in Haemophilia-A in USA (Parenteral)
  • 28 Nov 2024 No recent reports of development identified for preclinical development in Phenylketonuria in USA (Parenteral)
  • 28 Nov 2024 No recent reports of development identified for research development in Gaucher's-disease in USA (Parenteral)

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