AGTC 501

Drug Profile

AGTC 501

Alternative Names: AGTC-501; rAAV2tYF-GRK1-RPGR

Latest Information Update: 19 Jan 2018

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At a glance

  • Originator Applied Genetic Technologies Corporation
  • Class Eye disorder therapies; Gene therapies
  • Mechanism of Action Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    Yes - Retinitis pigmentosa
  • New Molecular Entity Yes

Highest Development Phases

  • Phase I/II Retinitis pigmentosa

Most Recent Events

  • 01 Jan 2018 Phase-I/II clinical trials in Retinitis pigmentosa (In children, In adolescents, In adults, In the elderly) in USA (Intraocular) (NCT03316560)
  • 13 Sep 2017 AGTC plans a phase I/II trial for Retinitis pigmentosa (X-linked; In children, In adolescents, In adults, In the elderly) in USA in January 2018 (NCT03316560)
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