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SPK 3006

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Drug Profile

SPK 3006

Alternative Names: RG-6359; SPK-3006; SPK-GAA

Latest Information Update: 16 Aug 2024

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At a glance

  • Originator Spark Therapeutics
  • Class Gene therapies
  • Mechanism of Action Alpha glucosidase expression stimulants; Gene transference
  • Orphan Drug Status

    Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

    No
  • New Molecular Entity No

Highest Development Phases

  • Discontinued Glycogen storage disease type II

Most Recent Events

  • 16 Aug 2024 Discontinued - Phase-II for Glycogen storage disease type II in France (IV) (Roche pipeline, August 2024)
  • 16 Aug 2024 Discontinued - Phase-II for Glycogen storage disease type II in USA (IV) (Roche pipeline, August 2024)
  • 25 Apr 2022 Phase-II clinical trials in Glycogen storage disease type II in France (IV) as of April 2022 (Roche pipeline, April 2022)

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