Sinbaglustat - Idorsia Pharmaceuticals
Alternative Names: ACT-519276; OGT-2378Latest Information Update: 29 Aug 2023
At a glance
- Originator Idorsia Pharmaceuticals
- Class Piperidines; Small molecules
- Mechanism of Action GBA2 protein inhibitors; Glucosylceramide synthase inhibitors
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Phase I Lysosomal storage diseases
Most Recent Events
- 29 Aug 2023 Phase-I clinical trials in Lysosomal storage diseases (unspecified route) is ongoing (Idorsia Pharmaceuticals pipeline, August 2023)
- 28 Aug 2023 No recent reports of development identified for phase-I development in Lysosomal storage diseases in Unknown
- 19 Aug 2021 Phase-I development is ongoing for Lysosomal storage diseases (Idorsia pipeline, August 2021)