Drug Profile

Research programme: small molecule therapeutics - PTC Therapeutics/CHDI

Alternative Names: Small molecule therapeutics - CHDI/PTC Therapeutics

Latest Information Update: 28 May 2022

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At a glance

Orphan Drug Status

Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.

No
New Molecular Entity Yes

28 May 2022 No recent reports of development identified for preclinical development in Huntington's-disease in USA (PO)
13 Jan 2020 PTC Therapeutics intends to file an investigational new drug (IND) application for Huntington disease in late 2020
04 Apr 2018 PTC Therapeutics and CHDI Foundation agree to co-develop small-molecule therapeutics for Huntington's disease

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