LYS FXS01
Alternative Names: Fragile X syndrome gene therapy - Lysogene; FXS01; LYS-FXS01Latest Information Update: 22 Apr 2022
At a glance
- Originator Conectus Alsace; Institute of Genetics and Molecular and Cellular Biology
- Class Gene therapies; Neuroprotectants
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Fragile X syndrome