Research programme: RNA base editor therapeutics - Beam Therapeutics
Latest Information Update: 28 Jun 2022
At a glance
- Originator Beam Therapeutics
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- No development reported Sickle cell anaemia
Most Recent Events
- 28 Jun 2022 No recent reports of development identified for research development in Sickle-cell-anaemia in USA (Parenteral)
- 12 Aug 2020 Beam Therapeutics and Boston Childrens Hospital agree to co-develop disease-specific therapies using base editing technology for sickle cell disease, paediatric leukaemias and other indications
- 31 Oct 2019 Beam Therapeutics and Prime Medicine enter into an agreement for the development of prime editing technology for various purposes, including for the treatment of sickle cell disease