Research programme: AAV vector based gene therapies - Abeona Therapeutics
Alternative Names: AIM™ vectorsLatest Information Update: 02 Apr 2024
At a glance
- Originator University of North Carolina at Chapel Hill
- Developer Abeona Therapeutics
- Class Gene therapies
- Mechanism of Action Gene transference
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity No
Highest Development Phases
- Preclinical Eye disorders
- No development reported CNS disorders; Fabry's disease; Glycogen storage disease type II
Most Recent Events
- 18 Mar 2024 Abeona Therapeutics files for patent protection with national authorities of US, Europe and other geographical regions for a second patent family directed to certain AAV capsids
- 18 Mar 2024 Abeona Therapeutics has patent protection for a patent family covering novel AAV capsids in US, Australia, Israel, Russia
- 28 Feb 2023 No recent reports of development identified for preclinical development in Fabry's-disease in USA (IV)