Research programme: PCSK9 inhibitors - Alexion AstraZeneca Rare Disease
Latest Information Update: 14 Feb 2022
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At a glance
- Originator SRX Cardio
- Developer Portola Pharmaceuticals
- Class Antihyperlipidaemics
- Mechanism of Action PCSK9 protein inhibitors
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Orphan Drug Status
Orphan designation is assigned by a regulatory body to encourage companies to develop drugs for rare diseases.
- New Molecular Entity Yes
Highest Development Phases
- Discontinued Hypercholesterolaemia